Chester County News and Community Website
WASHINGTON, D.C. — A seismic shift in pediatric medical care has arrived with the FDA’s approval of Ryoncil (remestemcel-L-rknd), a revolutionary therapy aimed at tackling the devastating condition known as steroid-refractory …
FDA Approves Groundbreaking Cell Therapy for Life-Threatening Pediatric Disease Read More
MALVERN, PA — Ocugen, Inc. (NASDAQ: OCGN) has received orphan medicinal product designation from the European Medicines Agency (EMA) for OCU410ST, a promising treatment for ABCA4-associated retinopathies including Stargardt disease, …
Ocugen Secures EMA Orphan Designation for OCU410ST, Advancing Stargardt Disease Treatment Read More
PHILADELPHIA, PA — Cabaletta Bio, Inc. (Nasdaq: CABA) announced that the U.S. Food and Drug Administration (FDA) has awarded Orphan Drug Designation (ODD) to its investigational therapy, CABA-201. This designation …
Cabaletta Bio Receives FDA Orphan Drug Designation for Innovative Autoimmune Disease Therapy Read More